Two people with cystic fibrosis dating each other 1on1 dating
In addition, patients on CFTR drugs are still experiencing long-term lung function decline – this needs to be addressed via alternative drug mechanisms.”“When the gene was discovered everyone thought that gene therapy for cystic fibrosis should be straightforward, but even though the discovery was 30 years ago, there is still no gene therapy available to cystic fibrosis patients,”“Not long after the discovery of the cystic fibrosis gene there were many research groups and biotech companies interested in developing a gene therapy.
After many clinical trials showed that none were successful in cystic fibrosis patients, many groups lost interest.”Gill, however, has not given up on this goal.
While the original version made use of tiny fat droplets to carry the DNA, the new one makes use of a hybrid virus.
But a new generation of genetic treatments might soon emerge thanks to CRISPR/Cas9 gene editing.Without chloride to attract water, the mucus that surrounds the cells in many organs becomes thick and sticky.The main organ affected is the lungs, where the mucus clogs airways and makes them prone to infection and inflammation.This technology could yield results that are much more accurate at predicting how the human body will behave under different conditions and how it will react to experimental drugs.It could also help patients with rare forms of cystic fibrosis be prescribed a personalized treatment.